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Mendeliome v2.0 RACGAP1 Gene migrated from ENSG00000161800 to ENSG00000161800 (gene set migration)
Mendeliome v1.4967 RACGAP1 Zornitza Stark Publications for gene: RACGAP1 were set to 34818416
Mendeliome v1.4966 RACGAP1 Zornitza Stark Classified gene: RACGAP1 as Green List (high evidence)
Mendeliome v1.4966 RACGAP1 Zornitza Stark Gene: racgap1 has been classified as Green List (High Evidence).
Mendeliome v1.4965 RACGAP1 Rylee Peters changed review comment from: PMID 36200420The study adds three unrelated families with autosomal recessive congenital dyserythropoietic anemia type III caused by homozygous missense RACGAP1 variants (p.Pro432Ser and p.Thr220Ala, the latter present in two families). Variant‑specific functional rescue in patient CD34⁺ erythroid cells and orthogonal HeLa knock‑down/ rescue assays demonstrate a loss‑of‑function mechanism.

PMID 36200420 Reports an additional 3 individuals from 3 families with autosomal recessive RACGAP1 missense variants presenting with congenital dyserythropoietic anemia type III (macrocytic anemia, multinucleated erythroblasts, hepatosplenomegaly). Variants are homozygous missense (p.Pro432Ser, p.Thr220Ala); functional studies in patient CD34+ erythroid cells and HeLa cells demonstrate rescue by wild‑type RACGAP1, supporting loss‑of‑function as disease mechanism.; to: PMID 36200420 Reports an additional 3 individuals from 3 families with autosomal recessive RACGAP1 missense variants presenting with congenital dyserythropoietic anemia type III (macrocytic anemia, multinucleated erythroblasts, hepatosplenomegaly). Variants are homozygous missense (p.Pro432Ser, p.Thr220Ala); functional studies in patient CD34+ erythroid cells and HeLa cells demonstrate rescue by wild‑type RACGAP1, supporting loss‑of‑function as a disease mechanism.
Mendeliome v1.4959 RACGAP1 Rylee Peters reviewed gene: RACGAP1: Rating: GREEN; Mode of pathogenicity: None; Publications: 36200420; Phenotypes: Anemia, congenital dyserythropoietic, type IIIb, autosomal recessive, MONDO:0030711; Mode of inheritance: BIALLELIC, autosomal or pseudoautosomal
Mendeliome v0.11512 RACGAP1 Zornitza Stark Marked gene: RACGAP1 as ready
Mendeliome v0.11512 RACGAP1 Zornitza Stark Gene: racgap1 has been classified as Red List (Low Evidence).
Mendeliome v0.11512 RACGAP1 Zornitza Stark gene: RACGAP1 was added
gene: RACGAP1 was added to Mendeliome. Sources: Expert Review
Mode of inheritance for gene: RACGAP1 was set to BIALLELIC, autosomal or pseudoautosomal
Publications for gene: RACGAP1 were set to 34818416
Phenotypes for gene: RACGAP1 were set to Anaemia, congenital dyserythropoietic, type IIIb, autosomal recessive 619789
Review for gene: RACGAP1 was set to RED
Added comment: Single affected individual reported.
Sources: Expert Review